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Clinical Trials

Clinical Research

Clinical research is medical research involving people. There are two different types of research: ​

  • Clinical trials are research studies performed on people focusing on a medical, surgical, or behavioral intervention. These help researchers determine if a new treatment, such as a new drug, diet, or medical device (eg. implants, etc.), is safe and effective in people. Often, a clinical trial is used to figure out if a new treatment is more effective and/or less harmful than the current standard of care.

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  • Non-interventional research is very important to pave the way for future clinical trials. These studies involve gathering information and collecting physiological and biomarker data, which are all essential to help understand the disease mechanism and to develop new treatments.

Spinocerebellar Ataxia Studies

NAF-funded National History Study of SCA

Who is this study for? 

SCA 1,2,3,7,8,10 diagnosis

How long will I need to participate? 

5 Years 

Single Patient 3-year Study for Troriluzole

Who is this study for?

SCA 3

How long will I need to participate?

3 Years

What is the treatment being studied? 

Troriluzole or Placebo Tablet, taken by mouth

ENGAGE Ataxia

Who is this study for?

SCA diagnosis with medical clearance to exercise

What is the treatment being studied? 

Physical Exercise

PRIME Ataxia

Who is this study for?

Ages 18-85; diagnosed with SCA

What is the treatment being studied? 

Physical Exercise

Essential Tremor Studies

A Phase II, Double-Blind, Placebo-controlled, Dose-response Study of SAGE-324 for the Treatment of Essential Tremor 

Who is this study for? 

ET duration at least 3 years; main symptoms is BUE action tremor, moderate to severe ET 

How long will I need to participate? 

90 days

What is the treatment being studied? 

SAGE-324 or Placebo Tablet, taken by mouth

A Phase III, Double-blind, Placebo-controlled, Dose-response Study of SAGE-324 for the Treatment of Essential Tremor 

Who is this study for?

Participated in SAGE-202

How long will I need to participate?

Years

What is the treatment being studied? 

SAGE-324 or Placebo Tablet, taken by mouth

The Essential Tremor Rating Assessment Scale Patient-Reported Outcome

Who is this study for?

Diagnosed with ET; ET duration at least 3 years; main symptoms is BUE action tremor

How long will I need to participate?

1 Month

What is the treatment being studied? 

N/A; observational

Multiple System Atrophy Studies

A Phase II Randomized, Double-Blind, Placebo-controlled Study of ATH434 in Multiple System Atrophy

Who is this study for? 

Ages 30-75; with motor symptoms duration of less than 4 years. 

How long will I need to participate? 

52 Weeks

What is the treatment being studied? 

ATH434 or Placebo Tablet, taken by mouth

A Phase III, Multi-center, Randomized Withdrawal and Long-Term Extension Study of Ampreloxetine for the Treatment of Symptomatic Neurogenic Orthostatic Hypotension in Participants with Multiple System Atrophy

Who is this study for?

Ages 30+; diagnosed with MSA-P or MSA-C, neurogenic Orthostatic Hypotension required with BP >/ 20 mmHg (systolic) or >/10 mmHg (diastolic) within 3 minute standing.

How long will I need to participate?

2.5 Years

What is the treatment being studied? 

Ampreloxetine or Placebo Tablet, taken by mouth

A Phase II, Double-blind, Placebo-controlled, Parallel-group Study to Assess the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Potential Efficacy with Multiple Doses of ONO-2808 in Patients with Multiple System Atrophy (MSA)

Who is this study for?

Ages 30-80; diagnosed with MSA-C or MSA-P; motor symptoms duration of less than 5 years; ability to ambulate 10 steps roundtrip

How long will I need to participate?

34 Weeks

What is the treatment being studied? 

ONO-2808 or Placebo Tablet, taken by mouth

Ataxia Studies

Caregiver of Ataxia Questionnaire

Who is this study for? 

Ataxia diagnosis and caregiver  

How long will I need to participate? 

One time

What is the treatment being studied? 

N/A, observational; one time questionnaire administered to both caregiver and patient

A National Study Examining Biomarkers for Ataxia and Multiple System Atrophy

Who is this study for?

Ages 18+; diagnosed with MSA

How long will I need to participate?

Years

What is the treatment being studied? 

N/A; observational study

Iowa Gambling Task

Who is this study for?

Patients diagnosed with any Ataxia

What is the treatment being studied? 

N/A; observational

Parkinson Disease Studies

A Phase II, Randomized, Double-blind, Placebo-controlled, Flexible-dosing, Parallel-group, Multicenter Study of the Efficacy and Safety of Suvecaltamide in the Treatment of Moderate to Severe Residual Tremor in Participants with Parkinson's Disease

Who is this study for? 

Ages 40-80; PD with severe residual tremor; optimized on PD meds

How long will I need to participate? 

23 Weeks

What is the treatment being studied? 

Suvecaltamide or Placebo Tablet, taken by mouth

For more information or questions about clinical research and ongoing trials,

please call us at (212) 305-5779.

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